Correction: Disease and patient characteristics in NP-C patients: findings from an international disease registry
نویسندگان
چکیده
Author details Mayo Clinic, Rochester, MN, USA. Villa Metabolica, ZKJM, MC, University of Mainz,, Mainz, Germany. Academic Medical Centre, University of Amsterdam, Amsterdam, The Netherlands. Actelion Pharmaceuticals Ltd, Allschwil, Switzerland. Numerus Ltd, Wokingham, UK. INSERM Unit 820, Lyon, France. Fundació Hospital Sant Joan de Déu, Barcelona, Spain. Department of Neurology, Mayo Clinic, 200 First Street SW, Rochester, MN 55905, USA.
منابع مشابه
Disease and patient characteristics in NP-C patients: findings from an international disease registry
BACKGROUND Niemann-Pick disease type C (NP-C) is a rare neurovisceral disease characterized by progressive neurodegeneration and premature death. We report data recorded at enrolment in an ongoing international NP-C registry initiated in September 2009 to describe disease natural history, clinical course and treatment experience of NP-C patients in clinical practice settings. METHODS The NPC ...
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عنوان ژورنال:
دوره 8 شماره
صفحات -
تاریخ انتشار 2013